Sequential Use of Novel
At
Agents in I d
n ucti
tion Th
Therapy
for Multiple My
pyeloma
Joan Bladé
XII International Myeloma Workshop
Washington, March 1, 2009

CP1123175-17

Survival from Onset of Treatment of
Multiple Myeloma
100
80
60
Placebo
Surviving
(%)
40
20
Urethane
0
0
10
20
30
40
50
Months
Holland, et al., 1966, Blood 27(3):335
CP1123175-18

MM. First Report on
Melphalan Therapy*
· Evaluation of new chemotherapeutic agents
in the treatment of multiple myeloma. L-
Phenylalanine mustard (NSC-8806)
* Bergsagel DE
DE et
et al
al. Cancer Chemother Rep
Rep 1962; 21: 87 99
-
.

MM. First Trial on Cyclophosphamide
Therapy*
· Ml
Mul il
tiple myeloma. A
l
na ysis of
l
cyc
h
op osphamid
ide
therapy in 165 Patients
* Korst DR et al (by the Midwest Cooperative
Chemotherapy Group). JAMA 1964; 180: 758 762
-
.

MM. Melphalan vs Cyclophosphamide
Trials*
·No significant differences in response rate
and overall survival
* Rivers SL and Patno ME. JAMA 1969; 207:1328-1334.
Witts LI et al (MRC trial)
trial). Br Med J 1971; 1:640
1:640 641
-
.

A Comparison of the Effect of
Prednisone (PDN) and a Placebo
Placebo in
the Treatment of Multiple Myeloma*
PDN
(40 mg/d
mg/d x
Placebo
p value
24 weeks)
No. patients
25
22
Serum globulin
28%
4%
0.036
decrease >15
>15 g/L
Significant Hb
26%
0%
0.001
* Mass RE. Cancer Chemother Rep 1962; 46:257-9.

Treatment for MM: Combination
Chemotherapy with Diff
Dif erent
Melphalan Dose Regimens *
Nº. of
Response
Regimen
patients
p
rate
Daily melphalan
35
19%
Intermittent melphalan
69
35%
Melphalan + alternate
alternate day PDN
28
65%
Melphalan + concurrent PDN
51
73%
* Alexanian R et al. JAMA 1969; 208:1680-5.

Combination Chemotherapy
Regimens Compared with MP
VBMCP
VCMP/VBAP
VBMCP/VBAD
VAD-like
ABCM


ASCT: Standard of Care for Younger Patients
ith
w
MM since 1990s
Patients Eligible and Non-eligible for ASCT

PATIENTS ELIGIBLE FOR HDT/ASCT

ASCT in MM:
Induction with Old Drugs (I)
· CR rate 35%
· Longer EFS
· Longer OS in some studies

ASCT in MM with Induction with
Old Drugs
· Long term outcome
­ Total Therapy I: 16/231 patients in continued
CR after a median follow-up of 12 y
pyrs*
­ Single ASCT: 11/95 patients in
in continued
continued CR
from 8 to 15 yrs**
*Barlogie et al, BJH 2007
** Rovira et al, EBMT Meeting 2009

Pre and Post-ASCT CR Rate with Novel
Id
Inducti
tion R
i
eg mens*
Regimen
Pre-ASCT
Post-ASCT
Thal/Dex
6%
23-34%
Vel/Dex
12%
33%
PAD
PA -
D 1
24%
43%
VTD
21-30%
43-49%
Total Therapy III**
-
56% at 2 yrs
*Cavo t
e l
a , ASH 2008; R i
os ñ
iñ l
o t
e l
a , ASH 2008; R i
os ñ
iñ l
o t
e l
a , JCO 2007;
Popat et al, BJH 2008; Barlogie et al, BJH 2007.
**VTD-PACE + Tandem ASCT + VTD/TD

Multidrug Pre-ASCT Induction (VTD,
VRD, PAD, VTD-PACE) or Gentle
Induction (i.e., alternating VEL/DEX)?
· Longer EFS?
· Longer OS?
· Superior long term
-
outcome (cure rate)?
rate)?

PATIENTS NON-ELIGIBLE FOR HDT/ASCT

Expanding Treatment Options for Front-
line Therapy of Eld
Eld l
er y P ti
a ents with
ith MM
Alkylating agent-based
Dexa-based
·
MPT (GIMEMA, IFM,
NMSG, HOVON)
·
Thal/Dex (ECOG,
Celgene 003,
· MPV (PETHEMA,
CEMSG)
VISTA)
· L/
Len D
/Dex (SWOG
· MPR (GIMEMA)
(SWOG,
ECOG, Others)
· CTD (MRC IX)

Unprecedented CR Rate with Novel plus Old
Drugs in Non-transplant Candidates
Regimen
CR rate (%)
MPT
1,2
MPT
15
MPR
3
24
MPV
4
30
Rev/Dex
5 or BIRD6
22-37
1
Palumbo et al, Lancet 2006
5
Lacy et al, Mayo Clin Proc 2007
2
Facon et al, Lancet 2007
6
Niesvizky et al,
y, Blood 2008
3
Palumbo et al, JCO 2007
4
San Miguel et al, NEJM 2008

MM. Impact on
o Su
S rviv
u
al of
o Fron
o t-line Treatment
with Novel Agents in Elderly Patients
· Longer EFS/PFS
· Longer OS in some studies
· Long-term outcome?
· Cure rate?

Impact of novel agents on outcome
in newly diagnosed
diagnosed disease
Overall survival
survival from
from diagnosis
diagnosis
1.0
1971-76
1977-82
08
0.8
1983 88
-
1989-94
1994-00
0.6
2001-06
vival
Sur
0.4
0.2
0.0
0
20
40
60
80
100
120
140
Time
Kumar et al. Blood 2008; 111: 2516­20

Improvements in survival of young
patients
Period estimates of 10-yr survival by major age groups in defined calendar
periods
50
45
(%) 40
<50
40
35
30
50­59
vesurvival 25
v
20
relati 15
60­69
10
70­79
-year
5
80+
10
5
0
1984­
1987­
1990­
1993­
1996­
1999­
2002­
1986
1989
1992
1995
1998
2001
2004
Calendar period
Improvements in survival for elderly patients expected with longer follow up of
ongoing trials
Brenner et al. Blood 2008;111:2521­26

Expected Long-term Survival of Patients
Diagnosed with Multiple Myeloma in
2006-2010*
· Projected 5-and 10 years relative survival
significantly improved in patients < 45 yrs.
· Survival projections hardly exceed estimates
from traditional survival analysis for older
patients
*Brenner et al, Haematologica, 2009

Tailored/Sequential Therapy for
Elderly Patients with MM
"Aggressive" disease
MPV
"Non-
Non aggressive"
aggressive disease
MPT
Poor cytogenetics
MPV
Renal failure
Ve
V l/Dex
e
History of peripheral neuropathy Len-based
Vl
Very e d
lderly
MPT (Th
(Th l
a 100
/d)
mg
Logistics
MPT/ Len-based

Disease Evolution
St
Sequen iti l
a Th
Therapy
45
M/P
40
Dex
35
Len/Dex
30
einot 25
-pr
Vel
Mm 20
ru
Se
15
10
IF-
IF
IF+
IF
EP+
5
0
7/98
9/99
9/00 8/01 11/02 9/03
4/04 10/04 10/05 10/06 10/07 10/08 2/09
Time

Current Expectations for Multiple
Myeloma
Are we closer to
Chronic??
or
Cure??
Future Workshops!!!